Enter your terms above and click the 'Search' button.

Showing articles 0 to 3 of 3 Filter Applied: gene therapy (Click to remove) Lentiviral Gene Therapy for Cerebral adrenoleukodystrophy NEJM 391:1302-1312,1358, Eichler,F.,et al, 2024 Hematopoietic Stem - and Progenitor-Cell Gene Therapy for Hurler Syndrome NEJM 385:1929-1940, Gentner, B.,et al, 2021 Muscular Dystrophies Lancet 394:2025-2038, Mercuri, E.,et al, 2019 Showing articles 0 to 3 of 3