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Showing articles 0 to 11 of 11 Filter Applied: gene therapy (Click to remove) Diagnosis and New Treatments in Muscular Dystrophies JNNP 80:706-714, Manzur,A.Y. &Muntoni,F., 2009 Muscular Dystrophies Lancet 394:2025-2038, Mercuri, E.,et al, 2019 Diagnosis and Therapy in Neuromuscular Disorders: Diagnosis and New Treatments in Mitochondrial Diseases JNNP 80:943-953, Rahman,S. &Hanna,M.G., 2009 Gene Therapy for Duchenne Muscular Dystrophy: Expectations and Challenges Arch Neurol 64:1236-1241, Rodino-Klapac,L.R.,et al, 2007 Myoblast Transfer in the Tratment of Duchenne's Muscular Dystrophy NEJM 333:832-838, 8711995., Mendell,J.R.,et al, 1995 Gene Therapy for Duchenne Dystrophy Ann Neurol 34:3-4, Engel,A.G., 1993 Myoblast Transfer in Duchenne Muscular Dystrophy Ann Neurol 34:8-18, Karpati,G.,et al, 1993 Lentiviral Gene Therapy for Cerebral adrenoleukodystrophy NEJM 391:1302-1312,1358, Eichler,F.,et al, 2024 Single-Dose Gene-Replacement Therapy for Spinal Muscular Atrophy NEJM 377:1713-1722,1786, Mendell, J.R.,et al, 2017 Spinal Muscular Atrophy A Timely Review Arch Neurol 68:979-984, Kolb, S.J.,et al, 2011 X Linked Adrenoleukodystrophy:Clinical Presentation, Diagnosis, and Therapy JNNP 63:4-14, vanGeel,B.M.,et al, 1997 Showing articles 0 to 11 of 11