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Showing articles 0 to 10 of 10 Filter Applied: gene therapy (Click to remove) Single-Dose Gene-Replacement Therapy for Spinal Muscular Atrophy NEJM 377:1713-1722,1786, Mendell, J.R.,et al, 2017 Parkinsons Disease NEJM 391:442-452, Tanner,C.M. & Ostrem,J.L., 2024 Current and Emerging Issues in Wilsons Disease NEJM 389:922-938, Roberts,E.A. & Schilsky, M.L., 2023 Muscular Dystrophies Lancet 394:2025-2038, Mercuri, E.,et al, 2019 Long-Term Safety and Tolerability of ProSavin, a Lentiviral Vector-Based Gene Therapy for Parkinsons Disease: A Dose Escalation, Open-Label, Phase 1/2 Trial Lancet 383:1138-1146,1107, Palfi, S.,et al, 2014 Spinal Muscular Atrophy A Timely Review Arch Neurol 68:979-984, Kolb, S.J.,et al, 2011 Glycogen-Storage Disease Type II eMedicine, May 2, Ibrahim,J. &McGovern,M., 2006 Tumor-free Survival of 7 Years After Gene Therapy for Recurrent Glioblastoma Neurol 61:270-271, Floeth,F.W,,et al, 2003 Neurovirological Methods and Their Applications JNNP 74:1016-1022, Kennedy,P.G.E., 2003 Gene Therapy for Neurologic Disease Arch Neurol 50:1252-1268, Suhr,S.T.&Gage,F.H., 1993 Showing articles 0 to 10 of 10