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Showing articles 0 to 2 of 2 Filter Applied: seizure,laughing as manifestation (Click to remove) Niemann-Pick Disease Type C Gene Reviews www.genereview.org, Bremova-Ertl,T. & Patterson, M., 2025 Intrathecal 2-hydroxypropyl-�-cyclodextrin Decreases Neurological Disease Progression in Niemann-Pick disease, type C1: a non-randomised, open-label, phase 1-2 trial Lancet 390:1758-1768, Ory, D.S.,et al, 2017 Showing articles 0 to 2 of 2