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Enzyme Replacement in Nervous Tissue After Allogeneic Bone-Marrow Transplantation for Fucosidoisis in Dogs
Lancet 2:772-774, Taylor,R.M.,et al, 1986
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bone marrow transplantation
enzyme,defect
fucosidosis
inborn errors of metabolism
lipid storage disorder of CNS
lysosomal storage disease
treatment of neurologic disorder
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