Hematopoietic Stem-Cell Transplantation in Globoid-Cell LeukodystrophyNEJM 338:1119-1126, Krivit,W.,et al, 1998
Protein Processing in Lysosomes:The New Therapeutic Target in Neurodegenerative DiseaseLancet 340:156-159, Mayer,R.J.,et al, 1992