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Showing articles 0 to 3 of 3 Filter Applied: gene therapy (Click to remove) Single-Dose Gene-Replacement Therapy for Spinal Muscular Atrophy NEJM 377:1713-1722,1786, Mendell, J.R.,et al, 2017 Spinal Muscular Atrophy A Timely Review Arch Neurol 68:979-984, Kolb, S.J.,et al, 2011 Gene Transfer for Neurologic Disease Neurol 63:2225-2232, Mendell,J.R. &Miller,A., 2004 Showing articles 0 to 3 of 3