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Showing articles 0 to 4 of 4 Filter Applied: gene therapy (Click to remove) Muscular Dystrophies Lancet 394:2025-2038, Mercuri, E.,et al, 2019 X Linked Adrenoleukodystrophy:Clinical Presentation, Diagnosis, and Therapy JNNP 63:4-14, vanGeel,B.M.,et al, 1997 Single-Dose Gene-Replacement Therapy for Spinal Muscular Atrophy NEJM 377:1713-1722,1786, Mendell, J.R.,et al, 2017 Spinal Muscular Atrophy A Timely Review Arch Neurol 68:979-984, Kolb, S.J.,et al, 2011 Showing articles 0 to 4 of 4