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Showing articles 0 to 3 of 3 Filter Applied: gene therapy (Click to remove) AAV9-Mediated Gene Therapy for Infantile-Onset Pompes Disease NEJM 392:2438-2446, 2477, Ma,X.,et al, 2025 Muscular Dystrophies Lancet 394:2025-2038, Mercuri, E.,et al, 2019 Glycogen-Storage Disease Type II eMedicine, May 2, Ibrahim,J. &McGovern,M., 2006 Showing articles 0 to 3 of 3