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Showing articles 0 to 4 of 4 Filter Applied: gene therapy (Click to remove) Muscular Dystrophies Lancet 394:2025-2038, Mercuri, E.,et al, 2019 Glycogen-Storage Disease Type II eMedicine, May 2, Ibrahim,J. &McGovern,M., 2006 AAV9-Mediated Gene Therapy for Infantile-Onset Pompes Disease NEJM 392:2438-2446, 2477, Ma,X.,et al, 2025 Current and Emerging Issues in Wilsons Disease NEJM 389:922-938, Roberts,E.A. & Schilsky, M.L., 2023 Showing articles 0 to 4 of 4