AAV9-Mediated Gene Therapy for Infantile-Onset Pompes DiseaseNEJM 392:2438-2446, 2477, Ma,X.,et al, 2025
Neonatal SeizuresNEJM 388:1692-1700, Ropper.A.H., 2023
Clinicopathologic Conference, Digitalis ToxicityNEJM 378:1931-1938, Case 15-2018, 2018