Duchenne Muscular Dystrophy
BMJ 368:L7012, Fox, H.,et al, 2020
Complex Regional Pain Syndrome
NEJM 393:2338-2348, Goebel,A., 2025
Amyotrophic Lateral Sclerosis
Lancet 400:1363-1380, Feldman, E.L.,et al, 2022
Non-Alzheimers Dementia 1 Frontotemporal Dementia
Lancet 386:1672-1682, Bang, Jee.,et al, 2015