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Nusinersen Versus Sham Control in Later-Onset Spinal Muscular Atrophy
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Long-Term Effects of Antidarsagene Autotemcel for Metachromatic Leukodystrophy
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Risdiplam in Presymptomatic Spinal Muscular Atrophy
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Single-Dose Gene-Replacement Therapy for Spinal Muscular Atrophy
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Safety and Diagnostic Value of Brain Biopsy in HIV patients: a Case Series and Meta-Analysis of 1209 Patients
JNNP 87:722-733, Lee, A.M.,et al, 2016
EMA401, An Orally Administered Highly Selective Angiotensin II Type 2 Receptor Antagonist, as a Novel Treatment for Postherpetic Neuralgia: A Randomised, Double-Blind, Placebo-Controlled Phase 2 Clinical Trial
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Evidence-based Guideline: Antiepileptic Drug Selection for People with HIV/AIDS
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Neurologic Outcomes and Adjunctive Steroids in HIV Patients with Severe Cerebral Toxoplasmosis
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Neurol 76:1372-1376, Sone, J.,et al, 2011
Enzyme Replacement Therapy With Agalsidase Alfa in Patients With Fabrys Disease: An Analysis of Registry Data
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Controlled Trial of High-Concentration Capsaicin Patch for Treatment of Painful HIV Neuropathy
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Epilepsy in Children
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