AAV9-Mediated Gene Therapy for Infantile-Onset Pompes Disease
NEJM 392:2438-2446, 2477, Ma,X.,et al, 2025
Progressive Proximal Weakness in a 56-year-old Man with Bone Pain
Neurol 93:939-944, Torabi,T.,et al, 2019
Neuromuscular Disorders in Severe Acute Respiratory Syndrome
Arch Neurol 61:1669-1673,1647, Tsai,L.-K.,et al, 2004