Lentiviral Gene Therapy for Cerebral adrenoleukodystrophy
NEJM 391:1302-1312,1358, Eichler,F.,et al, 2024
Clinicopath Conf., Adult Cerebral Form of X-Linked Adrenoleukodystrophy
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Follow-Up of 89 Asymptomatic Patients with Adrenoleukodystrophy Treated with Lorenzos Oil
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Proton MR Spectroscopic Imaging Predicts Lesion Progression on MRI in X-Linked Adrenoleukodystrophy
Neurol 58:901-907, Eichler,F.S.,et al, 2002
Long-term Effect of Bone-marrow Transplantation for Childhood-onset Cerebral X-linked Adrenoleukodystrophy
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Retinitis Pigmentosa
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