Intrathecal 2-hydroxypropyl-�-cyclodextrin Decreases Neurological Disease Progression in Niemann-Pick disease, type C1: a non-randomised, open-label, phase 1-2 trial
Lancet 390:1758-1768, Ory, D.S.,et al, 2017
Neurodevelopmental, Health, & Growth Status at Age 6 Years of Children with Birth Weights Less Than 1001 Grams
J Pediatr 118:768-777, Teplin,S.W.,et al, 1991
Neurologic Sequelae of Cardiac Surgery in Children
Am J Dis Child 141:309-312, Ferry,P.C., 1987