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Showing articles 0 to 3 of 3 Filter Applied: lysosomal storage disease (Click to remove) Intrathecal 2-hydroxypropyl-�-cyclodextrin Decreases Neurological Disease Progression in Niemann-Pick disease, type C1: a non-randomised, open-label, phase 1-2 trial Lancet 390:1758-1768, Ory, D.S.,et al, 2017 Psychosis in an Adolescent Girl: A Common Manifestation in Niemann-Pick Type C Disease Child Adolesc Pych Ment Health 8:20, Wouters,S.,et al, 2014 NEurologic Complications of Nonneuronopathic Gaucher's Disease Arch Neurol 48:1271-1272, Grewal,R.P.,et al, 1991 Showing articles 0 to 3 of 3